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Channel: Orphan Drug – New Drug Approvals
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Loncastuximab tesirine

Loncastuximab tesirine ZYNLONTA FDA APPROVED 2021/4/23 FormulaC6544H10048N1718O2064S52Exact mass147387.9585CAS1879918-31-6EfficacyAntineoplasitc, Anti-CD19 antibody  DiseaseDiffuse large B-cell...

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Ibrexafungerp citrate

Ibrexafungerp citrate アイブレキサフンジェルプクエン酸塩; FormulaC44H67N5O4. C6H8O7cas1965291-08-0free 1207753-03-4Mol weight922.1574 Brexafemme, fda approved 2021, 2021/6/1 Antifungal, Cell wall biosynthesis...

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Piflufolastat F 18 injection, Dcfpyl F-18

Piflufolastat F 18 injection Dcfpyl F-18 CAS 207181-29-0 PLAIN F 1423758-00-2  WITHOUT RADIO LABELC18 H23 F N4 O8, 441.4L-Glutamic acid,...

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Nanatinostat

Nanatinostat Tractinostat CHR-3996, CHR 3996, VRx 3996, C20H19FN6O2, 394.41 CAS 1256448-47-1 2-[(1α,5α,6α)-6-[[(6-Fluoro-2-q...

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MAX 40279

MAX 40279, EX-A4057 Max 4; MAX-40279; MAX-40279-001; MAX-40279-01 UNII-DL772G3NN7 2070931-57-4 C22H23FN6OS, 438.5...

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Vosoritide

PGQEHPNARK YKGANKKGLS KGCFGLKLDR IGSMSGLGC(Disulfide bridge: 23-39)...

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Efgartigimod alfa-fcab

DKTHTCPPCP APELLGGPSV FLFPPKPKDT LYITREPEVT CVVVDVSHED PEVKFNWYVDGVEVHNAKTK PREEQYNSTY RVVSVLTVLH QDWLNGKEYK CKVSNKALPA PIEKTISKAKGQPREPQVYT LPPSRDELTK NQVSLTCLVK GFYPSDIAVE WESNGQPENN...

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Olipudase alfa

HPLSPQGHPA RLHRIVPRLR DVFGWGNLTC PICKGLFTAI NLGLKKEPNV ARVGSVAIKLCNLLKIAPPA VCQSIVHLFE DDMVEVWRRS VLSPSEACGL LLGSTCGHWD IFSSWNISLPTVPKPPPKPP SPPAPGAPVS RILFLTDLHW DHDYLEGTDP DCADPLCCRR...

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Darinaparsin

SVG ImageIUPAC CondensedH-gGlu-Cys(Unk)-Gly-OHSequenceXXG Darinaparsin ダリナパルシン , Darvias JAPAN 2022 APPROVED, PMDA 2022/6/20...

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Danavorexton, TAK 925

Danavorexton,  TAK 925 2114324-48-8 Molecular FormulaC21H32N2O5SAverage mass424.554 Da 1-Piperidinecarboxylic acid, 3-[(methylsulfonyl)amino]-2-[[(cis-4-phenylcyclohexyl)oxy]methyl]-, methyl ester,...

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Valemetostat tosilate

Valemetostat tosilate バレメトスタットトシル酸塩 FormulaC26H34ClN3O4. C7H8O3SCAS1809336-93-3Mol weight660.2205 PMDA JAPAN approved 2022/9/26, Ezharmia 1,3-Benzodioxole-5-carboxamide,...

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ELRAGLUSIB

ELRAGLUSIB RN: 1034895-42-5UNII: ND1SOF0DLU, WHO 11553,  9-ING-41 1H-Pyrrole-2,5-dione, 3-(5-fluoro-3-benzofuranyl)-4-(5-methyl-5H-1,3-dioxolo(4,5-F)indol-7-yl)-...

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RELACORILANT

Relacorilant Molecular FormulaC27H22F4N6O3S Average mass586.561 Da CAS 1496510-51-0 Phase III UNII-2158753C7E 2158753C7E...

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